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NeuroBreak: Thumbs Down for Duchenne Drug; Fast-Track for Alzheimer’s Drug

NeuroBreak: Thumbs Down for Duchenne Drug; Fast-Track for Alzheimer’s Drug

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The FDA turned down PTC Therapeutics’ Duchenne muscular dystrophy drug ataluren, saying an additional clinical trial would be needed to prove the drug works. The agency had twice refused to file the application, saying the biotech had failed to put together a credible application after several trial failures. (Reuters/Endpoints News)

Alzheon has won fast-track status from the FDA for ALZ-801, a prodrug of tramiprosate. The company detailed clinical pharmacokinetics in a paper published last week, and has been looking to start a phase III trial of the drug for some time now. (FiercePharma)

President Trump’s commission on opioids will recommend establishing drug courts in every federal judicial district, adjusting reimbursement rates for addiction treatment, and streamlining federal funding for states and local governments to implement drug treatment and prevention programs. The final report will be released on Wednesday. (STAT News)

Swedish researchers have found a connection between concussion and multiple sclerosis. (New York Times)

Sanofi Genzyme is washing its hands of a Parkinson’s gene therapy being developed by Voyager. (Endpoints News)

Some highlights from the recent ECTRIMS-ACTRIMS meeting in Paris:

The Michael J. Fox Foundation gave genetic testing company 23andMe a $4-million grant to build a research cohort of “tens to hundreds of thousands” of patients with Parkinson’s disease. (GenomeWeb)

2017-10-31T12:00:00-0400

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